Pharmacological and toxicological studies in rare diseases are crucial for developing safe and effective treatments for conditions that affect a small number of people. These studies often face challenges due to limited patient populations and lack of data, but advances in genetic research and targeted therapies are improving our understanding and ability to manage these diseases. Collaborative efforts and specialized clinical trials are essential to ensure that patients with rare diseases receive the care they need.
7.1 Orphan Drugs and Their Development
7.2 Rare Disease Models and Animal Studies
7.3 Clinical Trials in Rare Diseases
7.4 Precision Medicine for Rare Diseases
7.5 Regulatory Pathways for Rare Disease Therapies
All accepted abstracts will be published in respective Allied Academies Journals.
Abstracts will be provided with Digital Object Identifier by
